Right heart dimensions, filling, and function in children on long-term parenteral nutrition: a transthoracic echocardiographic study
THE QUALITY OF LIFE IN CHRONIC BENIGN INTESTINAL FAILURE (IF) CHILDREN: THE ADOLESCENT’S POINT OF VIEW DURING THE TRANSITION TO THE ADULT WORLD
EFFICACY AND SAFETY OF MARALIXIBAT IN PATIENTS WITH PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS (MARCH-PFIC): A RANDOMIZED PLACEBO-CONTROLLED PHASE 3 STUDY
IMPACT OF MARALIXIBAT ON CHOLESTATIC PRURITUS IN YOUNG ADULTS AGED 16 YEARS AND OLDER WITH ALAGILLE SYNDROME
EFFICACY AND SAFETY OF ODEVIXIBAT IN PATIENTS WITH ALAGILLE SYNDROME: TOP-LINE RESULTS FROM ASSERT, A PHASE 3, DOUBLE-BLIND, RANDOMIZED, PLACEBO-CONTROLLED STUDY
EFFICACY AND SAFETY OF ODEVIXIBAT IN PATIENTS WITH ALAGILLE SYNDROME: INTERIM RESULTS FROM THE OPEN-LABEL, PHASE 3 ASSERT-EXT STUDY
ODEVIXIBAT THERAPY FOLLOWING LIVER TRANSPLANTATION IN PATIENTS WITH FIC1-DEFICIENT PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS: A RETROSPECTIVE CASE SERIES